A gene therapy trial has given hope to people with Haemophilia B. JackieLongc4 speaks to consultant in haemophilia Professor Pratima Chowdary, who helped carry out the research, and Elliot Mason, whose life has been transformed by the new treatment.
A new gene therapy has been developed that teaches their bodies to manufacture a missing protein that is vital to allow their blood to clot. In trials nine out of ten patients were effectively cured with a one-off infusion.
Jackie is joined by Professor Pratima Chowdary, consultant in haemophilia at London’s Royal Free Hospital, who helped carry out the research, and Elliot Mason, whose life has been transformed by this new gene therapy treatment.
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